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This trial is complete. It is no longer accepting participants.

NCT00010426

NCT00010426
Completed Not Applicable

Who may be able to join

Who might be able to join this trial:

  • You have been diagnosed with cystinosis, confirmed either by a lab test showing high levels of cystine in white blood cells, or by a doctor finding crystals in the front of your eye (cornea) using a special eye examination

  • You have a medical history that fits with a diagnosis of cystinosis

  • For the safety part of the study: You are between 1 and 50 years old, have been following the eye drop schedule and check-up routine from a related study (#86-El-0062), and your eye crystal levels have stayed the same or improved over the past year (including if no crystals are currently visible)

  • For the effectiveness part of the study: You are between 2 and 12 years old, your eye photographs show a crystal density score of at least 1.00, and you have been taking cysteamine (a medication for cystinosis) for at least the past 6 months

  • You are willing and able to have photographs taken of your cornea (the front of your eye)

Who may not be able to join:

  • For the effectiveness part of the study only: You have previously used cysteamine eye drops at any time

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

Trial details

Status
Completed
Phase
Not Applicable
Sponsor
FDA Office of Orphan Products Development
Registry
clinicaltrials_gov
Start date
1 December 1999

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 30 June 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

View original record on ClinicalTrials.gov