Phase 3 Haemophilia Trial, Completed NCT01425723 Sponsor: Bioverativ Therapeutics Inc. Condition: Haemophilia
Back to Haemophilia

Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial (NCT01425723) involved 120 children with haemophilia B — 27 from one earlier study and 93 from another — who received a clotting factor treatment called rFIXFc. The trial was measuring whether children developed "inhibitors" (antibodies that can block a clotting treatment from working), how often bleeding episodes occurred, and several other related things such as how much of the treatment was used and how doctors rated participants' responses to the treatment. The reported data shows that, for the primary outcome — whether any child developed inhibitors — the number was zero across all groups, meaning no confirmed inhibitor development was recorded in any participant. For bleeding rates (the average number of bleeding episodes per person per year), the reported figures varied depending on the treatment schedule and age group: children under six years on a regular preventive schedule had a reported rate of around 1.04 episodes per year, those aged six to under twelve years had around 1.14 episodes per year, and participants from the other study group had a reported rate of around 2.26 episodes per year on a similar schedule, with higher rates recorded for those on an on-demand (treat-when-bleeding) schedule. For spontaneous joint bleeds specifically, rates of zero were reported for the younger children on preventive schedules, with small numbers reported for some other groups. Doctors' assessments of how participants responded to the treatment were recorded across hundreds of visits; the reported data shows the large majority of responses fell into the top two categories on the four-point scale, with very few in the lower two categories, and none recorded in the lowest category. These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 3 Haemophilia Trial, Completed

NCT01425723
Completed Phase 3 🇦🇺 Australian site

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You must have already completed one of the following specific clinical trials: study 998HB102, study 9HB02PED, or another study involving the treatment called rFIXFc
  • You must be able to understand what the study involves and its risks, and be willing to sign and date a consent form agreeing to take part

Who may not be able to join:

  • People who have developed high levels of inhibitors (antibodies that block the treatment) at 5.00 BU/mL or above, as measured by a blood test (confirm with trial site if unsure what your levels are)

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 26 July 2026
Phase 3: approximately ~65% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Medical Director, Bioverativ Therapeutics Inc.

Australian sites

Research Site, Adelaide, South Australia
Research site, Parkville, Victoria
Research site, Murdoch, Western Australia
Research Site, Perth, Western Australia

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Completed
Phase
Phase 3
Sponsor
Bioverativ Therapeutics Inc.
Registry
ClinicalTrials.gov
Start date
8 December 2011
Est. completion
1 October 2017

Where this trial is recruiting

🇦🇺 Australia 🇧🇪 Belgium 🇧🇷 Brazil 🇨🇦 Canada 🇨🇳 China 🇫🇷 France 🇩🇪 Germany Hong Kong 🇮🇳 India 🇮🇪 Ireland 🇮🇹 Italy 🇯🇵 Japan 🇳🇱 Netherlands 🇵🇱 Poland 🇿🇦 South Africa 🇸🇪 Sweden 🇬🇧 United Kingdom 🇺🇸 United States

4 site(s) in Australia. Confirm current status and contact details directly with the trial site.

Primary endpoints

Number of Participants With Any Positive Inhibitor Development

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 26 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov