Phase 2 Primary Biliary Cholangitis Trial, Completed NCT02943460 Sponsor: Gilead Sciences Condition: Primary Biliary Cholangitis
Back to Primary Biliary Cholangitis

Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial (NCT02943460) looked at a medicine called cilofexor, tested at two different doses (100 mg and 30 mg), compared against a placebo (a dummy treatment with no active ingredient). A total of 52 people took part in the blinded phase — meaning participants did not know which treatment they were receiving — with 22 in the 100 mg group, 20 in the 30 mg group, and 10 in the placebo group. The trial's main focus was on monitoring and recording unwanted medical events (called adverse events) and unusual blood test results that occurred during the treatment period. The reported data shows that, during the blinded phase, 81.8% of participants in the cilofexor 100 mg group, 70.0% in the cilofexor 30 mg group, and 100% in the placebo group experienced at least one treatment-emergent adverse event (an unexpected medical event that appeared after starting the study drug). Serious adverse events — defined as events involving hospitalisation, life-threatening situations, death, or other significant medical concerns — were reported in 13.6% of the cilofexor 100 mg group, and 0% in both the cilofexor 30 mg and placebo groups. The reported data also shows that abnormal blood or laboratory test results were recorded for 90.9% of the 100 mg group, 85.0% of the 30 mg group, and 100% of the placebo group. Further breakdowns of laboratory abnormalities by severity level were also reported, though a full description of each category was not provided in the submitted data. These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 2 Primary Biliary Cholangitis Trial, Completed

NCT02943460
Completed Phase 2

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You have been diagnosed with Primary Sclerosing Cholangitis (PSC), confirmed by a special imaging scan of your bile ducts within the past 12 months
  • A specific liver enzyme in your blood called alkaline phosphatase (ALP) is above a certain elevated level
  • If you take a medication called ursodeoxycholic acid (UDCA), your dose has been the same for at least 12 months before joining and must stay the same throughout the trial; if you do not take it, you must not have taken it for at least 12 months before joining
  • If you take certain immune system medications (such as biologics, immunosuppressants, or steroid tablets), your dose has been stable for at least 3 months before joining and is expected to stay stable throughout the trial
  • Your liver scarring score (measured by a blood test called FibroSURE/FibroTest®) is below a certain level, or a recent liver biopsy within the past 12 months shows no cirrhosis (confirm with trial site)

Who may not be able to join:

  • A liver enzyme called ALT is more than 10 times the upper limit of normal in your blood test
  • Your blood bilirubin level (a measure of liver function) is more than twice the upper limit of normal
  • Your blood clotting measure (INR) is above 1.2, unless you are already on blood-thinning medication
  • You have a specific form called "small-duct PSC," where bile ducts appear normal on imaging but PSC is seen on a biopsy
  • You have another cause of liver disease, such as a viral, alcohol-related, inherited, or other autoimmune liver condition (those with fatty liver may still be eligible if there is no sign of a more serious form called NASH — confirm with trial site)
  • You have had a bile duct infection (ascending cholangitis) within the past 60 days
  • You currently have a drain or stent in your bile ducts
  • You have taken certain medications called fibrates or obeticholic acid within the past 3 months
  • You have advanced liver scarring (cirrhosis), shown by a biopsy, a history of serious liver complications (such as fluid buildup, confusion caused by liver disease, or bleeding from swollen veins), or a liver stiffness reading above 14.4 kPa on a FibroScan test
  • You currently have active inflammatory bowel disease (such as Crohn's disease or ulcerative colitis) with symptoms above a certain level of severity (confirm with trial site)

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 28 July 2026
Phase 2: approximately ~30% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

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Trial details

Status
Completed
Phase
Phase 2
Sponsor
Registry
ClinicalTrials.gov
Start date
29 November 2016
Est. completion
28 February 2018

Where this trial is recruiting

🇦🇹 Austria 🇨🇦 Canada 🇬🇧 United Kingdom 🇺🇸 United States

Primary endpoints

Percentage of Participants Experiencing Treatment-Emergent Adverse Events During the Blinded Phase; Percentage of Participants Experiencing Treatment-Emergent Serious Adverse Events During the Blinded Phase; Percentage of Participants Experiencing Treatment-Emergent Laboratory Abnormalities During the Blinded Phase

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov