Phase 3 Epilepsy Trial, Recruiting NCT04462770 Sponsor: Epygenix Condition: Epilepsy
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Phase 3 Epilepsy Trial, Recruiting

NCT04462770
Recruiting Phase 3

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • People who are 2 years of age or older at the time of giving consent to join the study.
  • People (or their parent or legal guardian) who are willing and able to sign a consent form before any study activities begin.
  • People who have been diagnosed with Dravet Syndrome (DS) whose seizures are not fully controlled by current seizure medications, and who also meet all of the following conditions:
    • Seizures began before 18 months of age
    • Development was normal when seizures first started
    • There is a history of at least one type of seizure that involves movement and can be counted
    • A brain scan (MRI) has shown no structural abnormalities in the outer layer of the brain (beyond any mild changes linked to the natural course of Dravet Syndrome)
    • A genetic test has confirmed a mutation in the SCN1A gene

Who may not be able to join:

  • People who have a known sensitivity, allergy, or previous exposure to the study drug clemizole HCl.
  • People who have taken part in another clinical trial involving an experimental drug or device within the past 90 days, or who plan to join another such trial during this study.
  • People whose seizures are caused by illicit drug use (including THC or non-prescription cannabis products), alcohol use, infection, tumours, certain nerve or brain diseases, or other progressive or metabolic conditions — rather than Dravet Syndrome itself.
  • People who are currently taking a medication called lorcaserin (though prior use is acceptable if at least 30 days have passed since the last dose).
  • People who are currently taking a medication called fenfluramine.
  • People who have had epilepsy surgery within the 6 months before the screening visit, or who have epilepsy surgery planned during the study period.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 23 July 2026
Phase 3: approximately ~65% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Amit Ray, MD, Harmony Biosciences Management, Inc.

Phone: +1 (312) 847-1289

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Phase 3
Sponsor
Epygenix
Registry
ClinicalTrials.gov
Start date
15 September 2020
Est. completion
1 April 2027

Where this trial is recruiting

🇨🇦 Canada 🇬🇪 Georgia 🇭🇺 Hungary 🇮🇳 India 🇵🇱 Poland 🇷🇴 Romania 🇪🇸 Spain 🇬🇧 United Kingdom 🇺🇸 United States

Primary endpoints

Percent Change in Countable Motor Seizures Per 28 Days (CMS-28) in the Titration Plus Maintenance Periods Relative to Baseline; European Union: Percent Change in Countable Motor Seizures Per 28 Days in the Maintenance Period Relative to Baseline

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 23 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov