Phase 3 Epilepsy Trial, Completed NCT04940624 Sponsor: Takeda Condition: Epilepsy
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Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial looked at a medicine called soticlestat compared to a placebo (a dummy treatment with no active ingredient) in people with a serious form of epilepsy. A total of 144 people took part — 71 in the placebo group and 73 in the soticlestat group. The trial measured how often participants experienced convulsive seizures (seizures involving shaking or loss of muscle control) over the course of the study, and whether the number of those seizures changed compared to before the trial started. The reported data shows that, on average, the placebo group had about an 8.6% reduction in convulsive seizures across the full treatment period, while the soticlestat group had about a 22.2% reduction. During a specific later phase called the "maintenance period," the placebo group showed roughly a 12% reduction and the soticlestat group showed roughly a 23.3% reduction. The reported data also shows that when looking at participants who had at least a 50% drop in their seizure rate — described in the trial as "responders" — about 9.9% of the placebo group met this threshold across the full treatment period, compared to about 27.4% of the soticlestat group. Caregivers were also asked to rate overall impressions of change; in the soticlestat group, about 4.5% rated the participant as "very much improved" and 27.3% as "much improved," compared to 1.5% and 11.8% respectively in the placebo group. These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 3 Epilepsy Trial, Completed

NCT04940624
Completed Phase 3 🇦🇺 Australian site

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You or your child has been formally diagnosed with Dravet Syndrome (DS).
  • There have been 12 or more convulsive (tonic-clonic or other major) seizures in the 12 weeks before the screening visit, and at least 4 convulsive seizures per 28 days during a 4- to 6-week observation period before the trial starts.
  • You or your child weighs at least 10 kg (about 22 lbs) at the first screening visit.
  • Seizures have not been fully controlled despite trying at least one anti-seizure medication, and you or your child is currently taking an anti-seizure medication or other standard treatment.
  • If taking artisanal (non-prescription) CBD products, the dose must have been stable for at least 4 weeks before screening, and the same product and dose must be kept throughout the study.
  • You or your child is currently taking between 0 and 4 anti-seizure medications at stable doses for at least 4 weeks before screening (certain medications like fenfluramine and prescription cannabidiol/Epidiolex count toward this limit where available).

Who may not be able to join:

  • You or your child has another serious or unstable medical condition — such as a significant heart, lung, liver, kidney, neurological, psychiatric, or other major health problem — that could affect participation in the study or make it harder to interpret the results (confirm with trial site).

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 21 July 2026
Phase 3: approximately ~65% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Study Director, Takeda

Australian sites

Queensland Childrens Hospital, South Brisbane, Queensland

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Completed
Phase
Phase 3
Sponsor
Registry
ClinicalTrials.gov
Start date
28 October 2021
Est. completion
11 April 2024

Where this trial is recruiting

🇦🇺 Australia 🇧🇷 Brazil 🇨🇦 Canada 🇨🇳 China 🇫🇷 France 🇩🇪 Germany 🇬🇷 Greece 🇭🇺 Hungary 🇮🇹 Italy 🇯🇵 Japan 🇱🇻 Latvia 🇳🇱 Netherlands 🇵🇱 Poland 🇷🇺 Russia 🇷🇸 Serbia 🇪🇸 Spain 🇺🇦 Ukraine 🇺🇸 United States

1 site(s) in Australia. Confirm current status and contact details directly with the trial site.

Primary endpoints

Percent Change From Baseline in Convulsive Seizure Frequency Per 28 Days During the Full Treatment Period; Percent Change From Baseline in Convulsive Seizure Frequency Per 28 Days During the Maintenance Period

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 21 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov