Gaucher Disease Trial, Recruiting
Who may be able to join
AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI
Who might be able to join this trial:
- You have been diagnosed with Gaucher disease, confirmed through blood tests and/or genetic testing, and you can be any age or gender.
- You (or your parent/legal guardian if you are under 18, or under 16 in the UK) are willing and able to sign a consent form agreeing to take part in the study.
Who may not be able to join:
- You are currently taking part in another clinical trial where neither you nor the doctors know which treatment you are receiving (known as a "blinded" trial), whether it involves a drug or a medical device.
Important: Always verify eligibility with the trial site directly before applying.
Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.
Contact this trial
Principal Investigator: Shire Study Physician, Shire
Phone: +1 866 842 5335
Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.
GP referral letter
Print a one-page summary to share with your doctor.
Trial details
Where this trial is recruiting
Primary endpoints
Number of Participants With Treatment-emergent Adverse Events (AEs) and Serious Adverse Events (SAEs); Number of Participants With Infusion-related Reactions (IRRs); Increase of Hemoglobin Concentration; Increase of Platelet Count; Decrease in Liver Volume; Decrease in Spleen Volume; Increase in Bone Mineral Density (BMD)
Can't join this trial?
Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.