Phase 3 Gaucher Disease Trial, Recruiting

Written by an AI model from ClinicalTrials.gov eligibility criteria and checked on a sample basis. Please confirm against the original criteria.

Who might be able to join this trial:

• You are 18 years old or older at the time of screening
• You have been diagnosed with Gaucher disease type 1
• Your hemoglobin (a measure of red blood cells) levels have been stable recently
• Your platelet count (cells that help blood clot) has been stable recently
• You have been continuously receiving ERT (enzyme replacement therapy) or SRT (substrate reduction therapy) for at least 2 years without any breaks

Who may not be able to join:

• You have been diagnosed with, or are suspected to have, Gaucher disease type 2 or type 3
• You have certain antibodies in your blood called AAVS3 neutralizing antibodies (confirm with trial site)
• You have abnormal lab results, health conditions, or other illnesses that could make participation unsafe (confirm with trial site)
• You are currently pregnant or breastfeeding
• You have previously had a bone marrow transplant, stem cell transplant, or any solid organ transplant (such as a kidney or liver transplant)
• You have previously received any type of gene therapy or cell therapy
• You have had your entire spleen surgically removed

Note: There are additional eligibility requirements not listed here — the trial site can provide the full details.

Important: Always verify eligibility with the trial site directly before applying.