Rare Disease Trial, Recruiting NCT03538639 Sponsor: National Heart, Lung, and Blood Institute (NHLBI) Condition: Rare Disease
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Rare Disease Trial, Recruiting

NCT03538639
Recruiting Not Applicable

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You must be between 2 and 100 years old.
  • Pregnant women who have a known or suspected medical condition being studied, or who become pregnant while already participating in the trial, may be eligible.
  • Pregnant women who are related to someone with the condition being studied (including spouses or partners) may be able to join for the purpose of collecting cord blood and tissue samples at the time of delivery only.

Who may not be able to join:

  • Healthy volunteers who are unable to give consent to participate.
  • Healthy volunteers who do not agree to have blood drawn, tissue studies performed, or samples stored for future research.
  • People who have thinking or memory difficulties (such as cognitive impairment) and who are not personally affected by the condition being studied.
  • People who have thinking or memory difficulties and who are not related to someone affected by the condition being studied.
  • Pregnant women who are both unaffected by the condition and unrelated to anyone with the condition.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 27 July 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Principal Investigator: Manfred Boehm, M.D., National Heart, Lung, and Blood Institute (NHLBI)

Phone: (301) 402-9841

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Not Applicable
Registry
ClinicalTrials.gov
Start date
30 July 2018
Est. completion
30 November 2027

Where this trial is recruiting

🇺🇸 United States

Primary endpoints

Rapid initiation of new, disease-specific investigations to enable the collection of data and biospecimens on affected subjects, their family members and healthy controls, and to assist in the generation of diagnoses and further the understandin...

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 27 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov