Phase 2 Endometriosis Trial, Completed NCT03654326 Sponsor: Merck Sharp & Dohme LLC Condition: Endometriosis
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Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial (NCT03654326) enrolled 187 participants — 94 in the gefapixant group and 93 in the placebo group (a placebo is a dummy treatment with no active ingredient, used for comparison). The trial was measuring changes in daily pelvic pain scores in people with endometriosis-related pelvic pain, using a scale of 0 to 10 where 0 meant no pain and 10 meant extremely severe pain. It also tracked how many participants experienced an unwanted medical event (called an adverse event) during the study, and how many stopped taking the study drug because of one. Most participants completed the study — 88 in the gefapixant group and 87 in the placebo group. The reported data shows that, for the main pain measure (average daily pelvic pain combining period-related and non-period-related pain, assessed roughly between weeks 4 and 8), scores in the gefapixant group decreased by an average of 2.2 points from their starting level, while scores in the placebo group decreased by an average of 1.7 points. For period-related pain alone, the reported decreases were 2.0 points (gefapixant) and 1.3 points (placebo). For pain not related to periods, the reported decreases were 2.3 points (gefapixant) and 1.8 points (placebo). In all cases, both groups showed a decrease from their starting scores. The reported data also shows that 53.2% of participants in the gefapixant group and 35.5% in the placebo group experienced at least one adverse event during the study period. Additionally, 3.2% of those in the gefapixant group stopped taking the study drug because of an adverse event, compared with 0.0% in the placebo group. These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 2 Endometriosis Trial, Completed

NCT03654326
Completed Phase 2 🇦🇺 Australian site

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You have been diagnosed with endometriosis through surgery (either keyhole surgery or open abdominal surgery).
  • You experience both period-related AND non-period-related pelvic pain that is moderate to severe (rated 5 or higher on a scale of 0–10).
  • You have been having natural, regular menstrual cycles before your first visit.
  • Your body mass index (BMI) falls between 18 and 40 at the time of your first visit.
  • You are not pregnant, not breastfeeding, and are willing to follow the trial's contraception guidelines.
  • You are willing to switch from your usual pain medication to only the pain relief options allowed within the study.

Who may not be able to join:

  • You have had your uterus removed (hysterectomy) and/or both ovaries removed (bilateral oophorectomy).
  • You have unexplained vaginal bleeding that has not been diagnosed.
  • You have long-term pain in other parts of the body (not the pelvis) that is unrelated to endometriosis and requires ongoing pain medication.
  • You have a significant gynaecological condition found during the screening process (confirm with trial site).
  • You have a history of a severe allergic reaction or serious skin reaction to sulfonamide antibiotics or other medicines containing sulfonamide.
  • You have a known allergy, sensitivity, or reason you cannot take the study drug gefapixant or any of its ingredients.
  • You have an allergy or intolerance to naproxen sodium (the rescue pain medication used in the trial), or you have previously had asthma, hives, or allergic reactions after taking aspirin or other anti-inflammatory pain medicines (such as ibuprofen).
  • Your endometriosis pain has previously not responded to certain hormone-based treatments, such as the combined contraceptive pill, or other hormonal therapies used for endometriosis (confirm with trial site).
  • You have a positive pregnancy test at any point before being enrolled in the trial.
  • You have needed to use opioid/narcotic pain medicines continuously for more than 2 weeks to manage your endometriosis pain within the last 6 months.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 28 July 2026
Phase 2: approximately ~30% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Medical Director, Merck Sharp & Dohme LLC

Australian sites

Paratus Clinical Kanwal ( Site 0004), Kanwal, New South Wales
Royal Hospital for Women ( Site 0008), Randwick, New South Wales
Holdsworth House Medical Practice ( Site 0009), Sydney, New South Wales
Royal Adelaide Hospital ( Site 0007), Adelaide, South Australia
Keogh Institute for Medical Research ( Site 0002), Nedlands, Western Australia

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

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Trial details

Status
Completed
Phase
Phase 2
Registry
ClinicalTrials.gov
Start date
11 September 2018
Est. completion
30 June 2020

Where this trial is recruiting

🇦🇺 Australia 🇨🇱 Chile 🇳🇿 New Zealand 🇵🇱 Poland Puerto Rico 🇷🇺 Russia 🇪🇸 Spain 🇺🇦 Ukraine 🇺🇸 United States

5 site(s) in Australia. Confirm current status and contact details directly with the trial site.

Primary endpoints

Change From Baseline in Average Daily Pelvic Pain Score During Treatment Cycle 2; Percentage of Participants Who Experienced an Adverse Event; Percentage of Participants Who Discontinued Study Drug Due to an Adverse Event

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov