Spinal Muscular Atrophy Trial, Recruiting NCT05204017 Sponsor: University of Alberta Condition: Spinal Muscular Atrophy
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Spinal Muscular Atrophy Trial, Recruiting

NCT05204017
Recruiting Not Applicable

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

If you are a patient:

  • You have been diagnosed with ALS (in any confirmed stage or type), ALS with frontotemporal dementia (ALS-FTD), primary lateral sclerosis (PLS), progressive muscular atrophy (PMA), or you carry a known ALS gene mutation even if you have no symptoms yet (confirm with trial site)
  • You have reached the legal age of adulthood in the province where you live or receive treatment
  • You are able to understand and agree to take part in the study on your own
  • You can read and communicate in English or French well enough to follow instructions and complete questionnaires

If you are a healthy volunteer (control participant):

  • You are between 40 and 80 years old, or you are within 3 years of the age of a patient already enrolled in the study
  • You have reached the legal age of adulthood in the province where you live or receive treatment
  • You are able to understand and agree to take part in the study on your own
  • You can read and communicate in English or French well enough to follow instructions and complete questionnaires

Who may not be able to join (healthy volunteers only):

  • You have a history of a neurological condition affecting the brain or nervous system, such as stroke, head injury, epilepsy, nerve damage, or muscle disease
  • You have been clinically diagnosed with a psychiatric condition such as depression or bipolar disorder, or you currently take medication for a psychiatric condition
  • You are unable to have an MRI scan due to a pacemaker or any other reason not allowed by the study centre's MRI safety rules
  • You experience significant claustrophobia (fear of enclosed spaces) that would prevent you from lying inside an MRI scanner for approximately one hour

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 28 July 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Principal Investigator: Sanjay Kalra, MD, University of Alberta

Phone: 514-398-6188

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Not Applicable
Registry
ClinicalTrials.gov
Start date
12 September 2021
Est. completion
1 December 2031

Where this trial is recruiting

🇨🇦 Canada

Primary endpoints

ALS Functional Rating Scale-Revised (ALSFRS-R); Forced Vital Capacity (FVC); Speech Testing; Neurological dysfunction as detected during standard neurological examination; Magnetic Resonance Imaging (MRI); Edinburgh Cognitive and Behavioural Screen (ECAS); ALS Assessment Questionnaire (ALSAQ-5); World Health Organization Quality of Life Questionnaire (WHO-QOL-BREF)

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov