Phase 4 Muscular Dystrophy Trial, Recruiting
Who may be able to join
AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI
Who might be able to join this trial:
- The participant must be between 1 month and 30 months old
- The participant must show signs of muscle weakness consistent with Duchenne muscular dystrophy, have a specific blood marker (creatine kinase) that is at least 20 times higher than the normal level, and have a confirmed gene change known to cause Duchenne muscular dystrophy
Who may not be able to join:
- The participant must not have previously been treated with a type of steroid medication called glucocorticosteroids (such as prednisone or deflazacort)
Important: Always verify eligibility with the trial site directly before applying.
Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.
Contact this trial
Principal Investigator: Anne Connolly, MD, Nationwide Children's Hospital
Phone: 614-355-3508
Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.
GP referral letter
Print a one-page summary to share with your doctor.
Trial details
Where this trial is recruiting
Primary endpoints
The change from baseline to 24 months for the Gross Motor Scaled Score.
Can't join this trial?
Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.