Phenylketonuria Trial, Recruiting
Who may be able to join
AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI
Who might be able to join this trial:
- You have been officially diagnosed with PKU (phenylketonuria) according to your local doctor's standard practice
- You are currently receiving, or are planning to start receiving, a treatment called pegvaliase within 30 days of signing up for the study (this includes people who previously received pegvaliase as part of earlier research studies)
- You (or your legal guardian or representative) are willing and able to sign a consent form after having the study fully explained to you, before any of your information is collected
Who may not be able to join:
- You have any condition that, in the opinion of the study doctor, might affect your ability to give informed consent or follow the study requirements (confirm with trial site)
- You are currently taking part in another clinical study involving an experimental treatment, device, or procedure
- You have already been enrolled in this particular study before, even if you left and want to re-join at a later date
- You are under 16 years of age and live in Germany
⚠️ Important: Always verify eligibility with the trial site directly before applying.
Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.
Contact this trial
Principal Investigator: Medical Director, MD, BioMarin Pharmaceutical
Phone: 1-800-983-4587
Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.
GP referral letter
Print a one-page summary to share with your doctor.
Trial details
Where this trial is recruiting
Primary endpoints
To quantify and characterize the risk of protocol-defined safety events in incident-users receiving pegvaliase for the treatment of PKU in a real¬ world setting.
Can't join this trial?
Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.