Phase 2 Sickle Cell Disease Trial, Recruiting NCT05953584 Sponsor: Forma Therapeutics, Inc. Condition: Sickle Cell Disease
Back to Sickle Cell Disease

Phase 2 Sickle Cell Disease Trial, Recruiting

NCT05953584
Recruiting Phase 2

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • A parent, legal guardian, or legal representative has given written permission for the patient to participate, and the patient themselves has also agreed to take part in an age-appropriate way
  • The patient is between 12 and 16 years old (inclusive) at the time of screening
  • The patient has a confirmed diagnosis of Sickle Cell Disease (SCD), based on past blood test results (no special genetic testing is required)
  • The patient has high blood flow speeds in certain brain arteries (measured at 170 cm/s or above on two separate occasions using a special ultrasound test), and has no history of stroke, mini-stroke, or severe blood vessel disease in the brain
  • The patient's hemoglobin (a measure of red blood cells) is between 6 and 9 g/dL at screening
  • If the patient is already taking a medication called hydroxyurea (HU), the dose must have been stable for at least 90 days before starting the study, with no expected need to change it (confirm with trial site)
  • Female patients who could become pregnant must agree to use an acceptable form of birth control and not donate eggs from the start of the study until 90 days after the last dose; male patients must also agree to use acceptable contraception and not donate sperm during this same period

Who may not be able to join:

  • Patients who are pregnant or currently breastfeeding
  • Patients who have a history of seizures or a seizure disorder
  • Patients who have had a stroke, a mini-stroke (TIA), a noticeable neurological weakness, or who show signs of severe blood vessel disease in the brain on scan results
  • Patients who have significantly low levels of certain blood cells (white blood cells, platelets, or reticulocytes — confirm with trial site)
  • Patients with severely reduced kidney function or who are on ongoing dialysis
  • Patients with significant liver problems, based on specific blood test results being too high (confirm with trial site)
  • Patients who have a serious active bacterial, fungal, parasitic, or viral infection currently requiring treatment — screening may be delayed until the infection has cleared
  • Patients who have HIV
  • Patients who have a known active Hepatitis B infection

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 23 July 2026
Phase 2: approximately ~30% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Clinical Transparency (dept. 2834), Novo Nordisk A/S

Phone: (+1) 866-867-7178

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Phase 2
Sponsor
Forma Therapeutics, Inc.
Registry
ClinicalTrials.gov
Start date
20 June 2023
Est. completion
20 September 2027

Where this trial is recruiting

🇮🇳 India Nigeria Oman

Primary endpoints

Change in the highest TAMMV in any of the L/R internal carotid artery [ICA] and L/R middle cerebral artery [MCA], whichever is highest, as measured by TCD

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 23 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov