Muscular Dystrophy Trial, Recruiting NCT06132750 Sponsor: Radboud University Medical Center Condition: Muscular Dystrophy
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Muscular Dystrophy Trial, Recruiting

NCT06132750
Recruiting Not Applicable

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • People who are willing and able to take part in measurements at the Radboudumc hospital in Nijmegen, or if visiting in person is not possible, participation through home visits may be arranged instead.
  • People who have a confirmed genetic diagnosis of LAMA2-related muscular dystrophy or SELENON-related myopathy, shown by two recessive disease-causing mutations in either the LAMA2 or SELENON gene.
  • People who have typical clinical and physical features of one of these conditions, along with a confirmed genetic diagnosis in a close family member (such as a parent, sibling, or child).
  • People who speak Dutch.

Who may not be able to join:

  • People who do not have a sufficient understanding of the Dutch language.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 28 July 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: +31611469112

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Not Applicable
Registry
ClinicalTrials.gov
Start date
6 October 2023
Est. completion
1 September 2026

Where this trial is recruiting

🇳🇱 Netherlands

Primary endpoints

Change of Motor Function Measure (MFM)-32 (older than 7 years) of MFM-20 (2 to 7 years old)

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov