Rare Disease Trial, Recruiting NCT06250595 Sponsor: Hospital Universitari Vall d'Hebron Research Institute Condition: Rare Disease
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Rare Disease Trial, Recruiting

NCT06250595
Recruiting Not Applicable

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You can be any age, from newborn to 100 years old, and any gender
  • You have been diagnosed with a rare hereditary blood disorder (called a Rare Haematological Disease, or RHD) as listed in the ORPHANET classification system (confirm with trial site)
  • You (or a parent/legal guardian if you are a minor) are willing and able to sign a consent form, as required by the laws in your country

Who may not be able to join:

  • You will not be able to join if you only carry a genetic trait for a recessive rare hereditary blood disorder without having the full condition yourself (confirm with trial site)

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 22 July 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Principal Investigator: María del Mar Manú Pereira, PhD, Vall d'Hebron Institut de Recerca / University Hospital Vall d'Hebron (VHIR / HUVH)

Phone: +34934893000

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Not Applicable
Sponsor
Hospital Universitari Vall d'Hebron Research Institute
Registry
ClinicalTrials.gov
Start date
1 July 2022
Est. completion
1 July 2037

Where this trial is recruiting

🇪🇸 Spain

Primary endpoints

Demography and epidemiology

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 22 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov