Phase 2 Sickle Cell Disease Trial, Recruiting NCT06481306 Sponsor: Bristol-Myers Squibb Condition: Sickle Cell Disease
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Phase 2 Sickle Cell Disease Trial, Recruiting

NCT06481306
Recruiting Phase 2

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

Healthy Volunteers (Cohort A):

  • People who are generally healthy, as assessed by the study doctor based on medical history and other checks.
  • Women who are not able to become pregnant — either because they have not had a period for at least 12 months (with no other medical explanation) and have hormone levels confirming this, or because they have had their uterus, both ovaries, or both fallopian tubes surgically removed.
  • People whose body weight is in a healthy range for their height, with a Body Mass Index (BMI) between 18.0 and 32.0.
  • People whose physical checks, vital signs, heart tracing (ECG), and blood test results show no significant health concerns.

People with Sickle Cell Disease (Cohort B):

  • People with a confirmed diagnosis of sickle cell disease of a specific genetic type: HbSS, HbSβ0-thal, or HbSβ+-thal.
  • For one part of the study: people who have had 4 or more painful crises in the past 12 months, or 2 or more in the past 6 months.
  • For another part of the study: people who have had between 2 and 15 painful crises in the past 12 months.
  • People who are generally able to carry out everyday activities with no or minimal limitations, as rated by a standard health scale (confirm with trial site).
  • People whose blood test results fall within specific ranges for red blood cells, white blood cells, platelets, and immature red blood cells (confirm with trial site for exact values).

Who may not be able to join:

Healthy Volunteers (Cohort A):

  • People with any significant medical condition, or any condition that could make it hard to interpret the study results.
  • People with any condition, including abnormal blood test results, that the study doctor considers would put them at unacceptable risk by joining.
  • People who have had major surgery, or have surgery planned, within 12 weeks before the study starts (except certain stomach or bowel surgery).

People with Sickle Cell Disease (Cohort B):

  • People with any significant ongoing or serious medical illness, an active or uncontrolled infection, or abnormal blood test results that would put them at unacceptable risk.
  • For one part of the study only: people who have had more than 6 severe painful crises requiring at least 24 hours in hospital within the past 12 months.
  • For one part of the study only: people who have had a serious lung complication called acute chest syndrome within the past 6 months.
  • People whose kidneys are not filtering blood well enough, as measured by a standard formula (confirm with trial site).

Both Groups:

  • People who are currently receiving regular red blood cell or platelet transfusions, or who have had a red blood cell transfusion within the past 28 days, or a platelet transfusion within the past 14 days before the study begins.
  • Other eligibility criteria set out in the study protocol may also apply (confirm with trial site).

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 26 July 2026
Phase 2: approximately ~30% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Bristol-Myers Squibb, Bristol-Myers Squibb

Phone: 855-907-3286

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Phase 2
Registry
ClinicalTrials.gov
Start date
17 July 2024
Est. completion
30 April 2028

Where this trial is recruiting

🇨🇦 Canada 🇫🇷 France 🇮🇹 Italy 🇬🇧 United Kingdom 🇺🇸 United States

Primary endpoints

Number of participants with adverse events (AEs); Number of participants with serious adverse events (SAEs); Number of participants with AEs meeting protocol-defined Dose Limiting Toxicity (DLT) criteria; Number of participants with AEs leading to discontinuation; Number of deaths; Proportion of participants achieving HbF ≥ 10%; Proportion of participants achieving HbF ≥ 20%; Proportion of participants achieving HbF ≥ 30%

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 26 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov