Muscular Dystrophy Trial, Recruiting

Written by an AI model from ClinicalTrials.gov eligibility criteria and checked on a sample basis. Please confirm against the original criteria.

Who might be able to join this trial:

• The patient (or their parent or legal guardian) must have signed a consent form, and the patient must agree to participate if old enough to do so.
• The patient must be aged from birth up to (but not including) 5 years old at the time of consent.
• The patient must have a confirmed diagnosis of LAMA2-RD, either through genetic testing showing two faulty copies of the LAMA2 gene (tested at an approved laboratory), or through a muscle biopsy showing absence of a specific protein called merosin along with at least one faulty copy of the LAMA2 gene.
• The patient must not have another confirmed genetic condition.
• The family must be willing to keep the patient's current exercise and/or physiotherapy routine the same throughout the study.
• The family must be willing to follow all study requirements, including attending all visits and completing all procedures.

Who may not be able to join:

• The patient has had an acute illness or hospital stay within the 30 days before signing consent.
• The patient has taken part in another clinical trial for LAMA2-RD within the past month, has used any other experimental treatment (including off-label use of a medication called Losartan) within the past 30 days, or has been in another clinical study within 30 days (or longer, depending on the medication involved) that the lead researcher believes could affect the results of this study.
• The patient has another significant health condition that, in the opinion of the lead researcher at the trial site, could make it harder to understand how LAMA2-RD is progressing.

Important: Always verify eligibility with the trial site directly before applying.