Spinal Muscular Atrophy Trial, Recruiting (NCT06839469)

Spinal Muscular Atrophy Trial, Recruiting NCT06839469 Sponsor: Columbia University Condition: Spinal Muscular Atrophy

Printed from Voxsanity (voxsanity.com.au) — NCT06839469 — Data sourced from ClinicalTrials.gov. Verify directly with the trial site before attending. Not medical advice.

Back to Spinal Muscular Atrophy

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

You have a confirmed genetic diagnosis of Duchenne Muscular Dystrophy (DMD), Spinal Muscular Atrophy (SMA), or you are a healthy volunteer (used as a comparison group)
You are able to walk at least 25 meters (about 82 feet) on your own, without help
If you have DMD: you are currently taking corticosteroid medication, or you started taking it within the last 3 months
If you have SMA: you have been on a stable dose of an FDA-approved SMA treatment for at least 6 months, or you are in an ongoing extension phase of a study treatment, or you have received gene replacement therapy

Who may not be able to join:

You use leg/foot braces, walking aids, or any mobility device (such as a wheelchair or scooter) to get around in the community
You have taken an experimental medication intended to treat a neuromuscular disease within the last 30 days
You have had an injury or surgery in the last 3 months that has affected the way you walk

⚠️ Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.

Last synced 28 July 2026

This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: 212-305-8916

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Voxsanity

Clinical trials and treatments, explained plainly · voxsanity.com.au

Date:

To: My Doctor

Re: Clinical trial enquiry

I am writing to enquire about the following clinical trial which may be relevant to my care:

Trial: NCT06839469

Sponsor: Columbia University

Phase: Not Applicable

Status: Recruiting

Condition: Spinal Muscular Atrophy

Trial contact: 212-305-8916

More information: https://clinicaltrials.gov/study/NCT06839469

Eligibility summary (AI generated)

Written by an AI model from ClinicalTrials.gov eligibility criteria and checked on a sample basis. Please confirm against the original criteria.

Who might be able to join this trial:

You have a confirmed genetic diagnosis of Duchenne Muscular Dystrophy (DMD), Spinal Muscular Atrophy (SMA), or you are a healthy volunteer (used as a comparison group)
You are able to walk at least 25 meters (about 82 feet) on your own, without help
If you have DMD: you are currently taking corticosteroid medication, or you started taking it within the last 3 months
If you have SMA: you have been on a stable dose of an FDA-approved SMA treatment for at least 6 months, or you are in an ongoing extension phase of a study treatment, or you have received gene replacement therapy

Who may not be able to join:

You use leg/foot braces, walking aids, or any mobility device (such as a wheelchair or scooter) to get around in the community
You have taken an experimental medication intended to treat a neuromuscular disease within the last 30 days
You have had an injury or surgery in the last 3 months that has affected the way you walk

⚠️ Important: Always verify eligibility with the trial site directly before applying.

Access in Australia: A treatment being studied in a clinical trial is generally not yet listed on the PBS. Where a medicine is not approved or not available through a trial, the TGA Special Access Scheme may allow a doctor to access unapproved therapeutic goods for individual patients. See voxsanity.com.au/sas-navigator/ for a plain English explainer.

This information was sourced from ClinicalTrials.gov via Voxsanity (data last synced 28 July 2026). It is not medical advice. Please verify the trial's current status directly with the trial site before acting.

Trial details

Status

Recruiting

Phase

Not Applicable

Sponsor

Columbia University

Registry

ClinicalTrials.gov

Start date

1 May 2024

Est. completion

30 December 2027

Where this trial is recruiting

🇺🇸 United States

Primary endpoints

Six Minute Walk Test; 10 Meter Walk/Run; Time Up and Go Test (TUG); Muscle Strength Testing with Hand-held Dynamometry (HHD); 30 Second Sit to Stand Test (30STS); Ankle Range of Motion; Knee Extension Range of Motion; Hip Extension Range of Motion

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov