Muscular Dystrophy Trial, Recruiting (NCT06924125)

Muscular Dystrophy Trial, Recruiting NCT06924125 Sponsor: Hospital Universitari Vall d'Hebron Research Institute Condition: Muscular Dystrophy

Printed from Voxsanity (voxsanity.com.au) — NCT06924125 — Data sourced from ClinicalTrials.gov. Verify directly with the trial site before attending. Not medical advice.

Back to Muscular Dystrophy

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

You have symptoms that match the condition AND genetic testing has found 2 faulty copies of the LAMA2 gene, OR a muscle biopsy has shown low levels of a protein called laminin alpha2 along with at least one faulty copy of the LAMA2 gene.
You (or your legal guardian) have signed a consent form agreeing to take part, and if you are 6 years old or older, you have also given your own agreement to join.

Who may not be able to join:

No specific exclusion criteria were listed in the official document (confirm with trial site).

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.

Last synced 27 July 2026

This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: +34934893156

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

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Voxsanity

Clinical trials and treatments, explained plainly · voxsanity.com.au

Date:

To: My Doctor

Re: Clinical trial enquiry

I am writing to enquire about the following clinical trial which may be relevant to my care:

Trial: NCT06924125

Sponsor: Hospital Universitari Vall d'Hebron Research Institute

Phase: Not Applicable

Status: Recruiting

Condition: Muscular Dystrophy

Trial contact: +34934893156

More information: https://clinicaltrials.gov/study/NCT06924125

Eligibility summary (AI generated)

Written by an AI model from ClinicalTrials.gov eligibility criteria and checked on a sample basis. Please confirm against the original criteria.

Who might be able to join this trial:

You have symptoms that match the condition AND genetic testing has found 2 faulty copies of the LAMA2 gene, OR a muscle biopsy has shown low levels of a protein called laminin alpha2 along with at least one faulty copy of the LAMA2 gene.
You (or your legal guardian) have signed a consent form agreeing to take part, and if you are 6 years old or older, you have also given your own agreement to join.

Who may not be able to join:

No specific exclusion criteria were listed in the official document (confirm with trial site).

Important: Always verify eligibility with the trial site directly before applying.

Access in Australia: A treatment being studied in a clinical trial is generally not yet listed on the PBS. Where a medicine is not approved or not available through a trial, the TGA Special Access Scheme may allow a doctor to access unapproved therapeutic goods for individual patients. See voxsanity.com.au/sas-navigator/ for a plain English explainer.

This information was sourced from ClinicalTrials.gov via Voxsanity (data last synced 27 July 2026). It is not medical advice. Please verify the trial's current status directly with the trial site before acting.

Trial details

Status

Recruiting

Phase

Not Applicable

Sponsor

Hospital Universitari Vall d'Hebron Research Institute

Registry

ClinicalTrials.gov

Start date

27 July 2021

Est. completion

1 July 2030

Where this trial is recruiting

🇪🇸 Spain

Primary endpoints

Change in Motor function Measurement (MFM32) score; Change in Motor Milestones; Change in Muscle Echogenicity by Muscle Ultrasound

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 27 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov