Sickle Cell Disease Trial, Recruiting (NCT06941389)

Sickle Cell Disease Trial, Recruiting NCT06941389 Sponsor: University of Rochester Condition: Sickle Cell Disease

Printed from Voxsanity (voxsanity.com.au) — NCT06941389 — Data sourced from ClinicalTrials.gov. Verify directly with the trial site before attending. Not medical advice.

Back to Sickle Cell Disease

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

Children and young people between the ages of 3 and 20 years old (up to 20 years and 11 months)
People diagnosed with sickle cell anemia (specifically the types known as HbSS or HbSβ0 thalassemia)
For one group in the study: children who are suitable candidates to receive a stem cell transplant from a matched family member (related donor)
For the other group in the study: children who are currently receiving non-transplant treatments to manage their sickle cell disease
The participant, or their parent or guardian, must agree to take part in the study by signing a consent form
Participants must be willing and able to attend the required check-ups and follow-up visits over the 3-year study period

Who may not be able to join:

Children younger than 3 years old or older than 20 years and 11 months
Children who do not have sickle cell anemia or a related condition
For the transplant group: children who are not suitable for a stem cell transplant, or who do not have a matching family member available as a donor
Children who are already taking part in another clinical trial that could affect the results of this study
Children who are unable to follow the study's requirements or attend the necessary appointments

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.

Last synced 22 July 2026

This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: 5852742345

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Voxsanity

Clinical trials and treatments, explained plainly · voxsanity.com.au

Date:

To: My Doctor

Re: Clinical trial enquiry

I am writing to enquire about the following clinical trial which may be relevant to my care:

Trial: NCT06941389

Sponsor: University of Rochester

Phase: Not Applicable

Status: Recruiting

Condition: Sickle Cell Disease

Trial contact: 5852742345

More information: https://clinicaltrials.gov/study/NCT06941389

Eligibility summary (AI generated)

Written by an AI model from the ClinicalTrials.gov eligibility criteria and checked on a sample basis. Please confirm against the original criteria.

Who might be able to join this trial:

Children and young people between the ages of 3 and 20 years old (up to 20 years and 11 months)
People diagnosed with sickle cell anemia (specifically the types known as HbSS or HbSβ0 thalassemia)
For one group in the study: children who are suitable candidates to receive a stem cell transplant from a matched family member (related donor)
For the other group in the study: children who are currently receiving non-transplant treatments to manage their sickle cell disease
The participant, or their parent or guardian, must agree to take part in the study by signing a consent form
Participants must be willing and able to attend the required check-ups and follow-up visits over the 3-year study period

Who may not be able to join:

Children younger than 3 years old or older than 20 years and 11 months
Children who do not have sickle cell anemia or a related condition
For the transplant group: children who are not suitable for a stem cell transplant, or who do not have a matching family member available as a donor
Children who are already taking part in another clinical trial that could affect the results of this study
Children who are unable to follow the study's requirements or attend the necessary appointments

Important: Always verify eligibility with the trial site directly before applying.

Access in Australia: A treatment being studied in a clinical trial is generally not yet listed on the PBS. Where a medicine is not approved or not available through a trial, the TGA Special Access Scheme may allow a doctor to access unapproved therapeutic goods for individual patients. See voxsanity.com.au/sas-navigator/ for a plain English explainer.

This information was sourced from ClinicalTrials.gov via Voxsanity (data last synced 22 July 2026). It is not medical advice. Please verify the trial's current status directly with the trial site before acting.

Trial details

Status

Recruiting

Phase

Not Applicable

Sponsor

University of Rochester

Registry

ClinicalTrials.gov

Start date

1 June 2024

Est. completion

1 October 2030

Where this trial is recruiting

🇨🇦 Canada 🇺🇸 United States

Primary endpoints

Health-Related Quality of Life as Measured by the Pediatric Quality of Life Inventory (PedsQL) Generic Core Scale (Parent-Proxy Report); Cognitive Function as Measured by the NIH Toolbox Cognitive Battery

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 22 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov