Muscular Dystrophy Trial, Recruiting
Who may be able to join
AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI
Who might be able to join this trial:
If your child has DMD or BMD (Duchenne or Becker Muscular Dystrophy):
- Your child is able to walk on their own at the time of screening
- Your child has been diagnosed with DMD or BMD confirmed through genetic testing
- A parent or guardian is able to give permission for their child to take part, and children aged 7 and older will also be asked for their own agreement to participate (if the medical team feels this is appropriate for the child's development)
- Your home has access to electricity and a freezer to use the provided device and store collected samples
If your child is a healthy volunteer (control participant):
- Your child is generally healthy and does not have DMD, BMD, or another serious long-term medical condition
- Your child is able to walk on their own without any assistive devices at the time of screening
- A parent or guardian is able to give permission for their child to take part, and children aged 7 and older will also be asked for their own agreement to participate (if the medical team feels this is appropriate for the child's development)
- Your home has access to electricity and a freezer to use the provided device and store collected samples
Who may not be able to join:
- Your child is unable to walk independently and requires a walking aid or assistive device
- Your child is female
- A parent or guardian is not available or able to provide consent for the child to participate
Important: Always verify eligibility with the trial site directly before applying.
Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.
Contact this trial
Principal Investigator: Sabrina Yum, MD, Children's Hospital of Philadelphia
Phone: 267-426-7786
Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.
GP referral letter
Print a one-page summary to share with your doctor.
Trial details
Where this trial is recruiting
Primary endpoints
Change in urinary NTFT (titin) after structured activity; Urinary NTFT (titin) relative during unstructured activity in home environment; Unstructured activity level as assessed by wearable activity device
Can't join this trial?
Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.