Phase 3 Muscular Dystrophy Trial, Recruiting
Who may be able to join
AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI
Who might be able to join this trial:
- You are a male who can walk and has been diagnosed with Duchenne muscular dystrophy (DMD), with a specific type of genetic change that could be helped by a treatment called "exon 51 skipping"
- You are able to get up from the floor in under 10 seconds, and this was confirmed at two separate check-up appointments
- You have been taking steroids (such as prednisolone or deflazacort) at a steady dose every day or on weekends for at least 6 months before joining, and you are expected to continue at that same dose during the study
Who may not be able to join:
- You have taken medication that suppresses your immune system (other than steroids) in the last 3 months
- You have used any medication (other than steroids) that could affect muscle strength or function in the last 3 months
- Your treatment for heart failure has been changed in the last 3 months
- You have received a drug called eteplirsen in the last week
- You have received other exon-skipping treatments, dystrophin-modifying therapies, or a drug called zeleciment rostudirsen in the last 6 months
- You have received a drug called givinostat in the last 3 months
- You have ever received gene therapy at any point in your life
Important: Always verify eligibility with the trial site directly before applying.
Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.
Contact this trial
Phone: +1-781-317-1919
Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.
GP referral letter
Print a one-page summary to share with your doctor.
Trial details
Where this trial is recruiting
Primary endpoints
Rise From Floor (RFF) velocity
Can't join this trial?
Data last synced from ClinicalTrials.gov: 26 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.