Rare Disease Trial, Recruiting NCT07039084 Sponsor: Murdoch Childrens Research Institute Condition: Rare Disease
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Rare Disease Trial, Recruiting

NCT07039084
Recruiting Not Applicable 🇦🇺 Australian site

voxsanity.com.au · Eligibility summary from public government registries · 18 August 2026 · not medical advice

Who may and may not be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who may be able to join

  • Your child is between 3 and 12 years old at the time of joining the trial
  • Your child has been diagnosed with a rare genetic disorder
  • Your child is able to tap on an iPad on their own or by copying someone else, and has adequate hearing (this is checked with a short screening test)
  • Your child speaks fewer than 50 words or phrases on their own, as confirmed by a specific assessment tool
  • Your child does not currently use a speech-generating device as their main way of communicating every day
  • Your child speaks English, or you as the parent/guardian are willing for therapy to be carried out in English, and you are able to complete parent questionnaires in English

Who may not be able to join

Each point below is a reason the trial team may not be able to accept someone. It is not a list of requirements to meet.

  • Your child has more than one genetic variation or condition (confirm with trial site)
  • Your child is very unwell or their condition has progressed significantly — for example, they have notable loss of vision, hearing, or fine motor skills, or they are too unwell to attend sessions regularly
  • Your child lives outside of the state of Victoria, Australia, as some appointments need to be attended in person
  • You or your child are unable or unwilling to provide written consent to participate in the trial

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 12 August 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: +61 (03) 8341 6458

Australian sites

Murdoch Children's Research Institute, Melbourne, Victoria
+61 (03) 8341 6458

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Recruiting
Phase
Not Applicable
Sponsor
Murdoch Childrens Research Institute
Registry
ClinicalTrials.gov
Start date
3 November 2025
Est. completion
1 May 2027

Where this trial is recruiting

🇦🇺 Australia

1 site(s) in Australia. Confirm current status and contact details directly with the trial site.

Primary endpoints

Changes in the frequency of target communicative act related to the patient-defined outcome determined at the beginning of the trial

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 12 August 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov