Rare Disease Trial, Not Yet Recruiting NCT07741747 Sponsor: Assistance Publique Hopitaux De Marseille Condition: Rare Disease
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Rare Disease Trial, Not Yet Recruiting

NCT07741747
Not Yet Recruiting Not Applicable

voxsanity.com.au · Eligibility summary from public government registries · 18 August 2026 · not medical advice

Who may and may not be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who may be able to join

  • Children under 18 years old.
  • People with a confirmed or suspected diagnosis of FHL (Familial Hemophagocytic Lymphohistiocytosis) or a related genetic condition that increases the risk of HLH (such as Griscelli Syndrome, Chédiak-Higashi Syndrome, XLP1, or XLP2), or a family history of a condition involving abnormal immune cell activation.
  • People who meet at least 5 of the following 8 medical criteria, as defined by the Histiocyte Society: fever; an enlarged spleen; abnormally high fat levels or low fibrinogen (a clotting protein) in the blood; evidence of immune cells attacking blood cells, found in a tissue sample; reduced or absent natural killer (NK) cell activity; a ferritin (iron-related protein) level of 500 µg/l or above; elevated levels of a specific immune marker called soluble CD25, or the presence of activated immune cells detected through specialised blood testing; or low counts in at least two types of blood cells (red blood cells, platelets, or white blood cells).
  • People covered by French social security.
  • People whose legal guardian(s) have signed the informed consent form for the trial.

Who may not be able to join

Each point below is a reason the trial team may not be able to accept someone. It is not a list of requirements to meet.

  • People aged 18 or older.
  • People who have a solid tumour, leukaemia, or lymphoma.
  • People covered under specific articles of the French public health code, including those under guardianship or curatorship, those deprived of liberty, and women who are pregnant or breastfeeding.
  • People who do not understand the French language.
  • People currently within an exclusion period from another research study at the time the consent form is signed.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 18 August 2026
This study is not part of the standard drug-approval phase pathway (for example an observational, device, behavioural, or registry study), so a phase success rate does not apply.

Contact this trial

Phone: 04 91 38 98 21

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Not Yet Recruiting
Phase
Not Applicable
Registry
ClinicalTrials.gov
Start date
1 October 2026
Est. completion
1 October 2028

Where this trial is recruiting

🇫🇷 France

Primary endpoints

Time (in days) from clinical suspicion to hematopoietic stem cell transplantation

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 18 August 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov