Rare disease
Friedreich Ataxia
Clinical trials recruiting in Australia for Friedreich Ataxia, a rare disease, as the public registries list them.
Also called: FA; FRDA; Friedreich's ataxia; Friedrich's ataxia; Friedreich spinocerebellar ataxia
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At a glance
4 trials recruiting in Australia
22 trials recruiting overseas
1-9 / 1 000 000 (Point prevalence, Greece, Validated) prevalence
Adolescent; Childhood age of onset
11 October 2026 date last checked
Trials in Australia
This Australian count is likely to be on the low side. It counts the trials this site files under this condition; the registry’s own search is broader and also returns closely related conditions, some of which have their own page here. If you are searching widely, check the registry as well — every trial below links to its own record.
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Recruiting Not a phased study
Study for people with Friedreich Ataxia
Where- Online Patient Enrollment System, Sydney — Recruiting
Who can join Age child, adult, older adult. Sex Anyone, regardless of sex. Healthy volunteers Not accepted.Sponsor Sanford HealthTimelineStarted 1 July 2010 Today 16 October 2026 Estimated completion 1 December 2100NCT01793168 · Checked 11 October 2026
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Recruiting Not a phased study
Study for people with Friedreich Ataxia
Where- Murdoch Childrens Research Institute, Parkville (VIC) — Recruiting
Who can join Age child, adult, older adult. Sex Anyone, regardless of sex. Healthy volunteers Accepted.Sponsor Friedreich's Ataxia Research AllianceTimelineStarted 28 June 2023 Today 16 October 2026 Estimated completion 28 January 2048NCT06016946 · Checked 11 October 2026
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Not yet recruiting Phase 1
Phase 1 study for people with Friedreich Ataxia
WhereNo Australian site on this record is listed as recruiting right now, even though the trial itself is open. Check with the site or the official record before travelling.
- Nucleus Network, Level 5, 89 Commercial Road, Melbourne (VIC) — this site's status is not stated on the record
Who can join Age 18 Years to 45 Years. Sex Anyone, regardless of sex. Healthy volunteers Accepted.Sponsor Design Therapeutics, Inc.TimelineStarted 1 February 2025 Today 16 October 2026 Estimated completion 1 September 2025Past estimated completion. The registry still lists this trial as open, and the date it gave for finishing has been and gone. Confirm with the official record before you act on it.
NCT06772870 · Checked 11 October 2026
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Recruiting Phase 2
Phase 2 study for people with Friedreich Ataxia
Where- Scientia Clinical Research Ltd, Sydney (NSW) — Recruiting
- Doherty Clinical Trials, East Melbourne (VIC) — Recruiting
- Nucleus Network, Melbourne (VIC) — Recruiting
Who can join Age 18 Years to 65 Years. Sex Anyone, regardless of sex. Healthy volunteers Not accepted.Sponsor Design Therapeutics, Inc.TimelineStarted 1 June 2025 Today 16 October 2026 Estimated completion 1 December 2026NCT06874010 · Checked 11 October 2026
Trials overseas
22 trials for this disease are open to new participants outside Australia, as ClinicalTrials.gov listed them on 11 October 2026. Voxsanity does not publish a page for any of them; the searches below reach them at the registry.
These overseas counts are likely too high. They come from the registry’s own search, which expands a condition name to related conditions, so some of the trials counted are for a different disease in the same family.
Search ClinicalTrials.gov Search the WHO registry portal Joining a trial overseas
Trials not shown here
Some Australian trials are registered only on the Australian New Zealand Clinical Trials Registry and are not shown here. Search them at Australian Clinical Trials.
Key facts
Orphadata Science: Free access data from Orphanet. © INSERM 1999. Available on https://www.orphadata.com. Used under CC BY 4.0. Source: Orphanet / Orphadata (orphadata.com).
About Friedreich Ataxia
The text below is reproduced exactly as its source published it. It has not been edited, shortened or rewritten.
Friedreich ataxia is an inherited disease that damages your nervous system. The damage affects your spinal cord and the nerves that control muscle movement in your arms and legs. Symptoms usually begin between the ages of 5 and 15. The main symptom is ataxia, which means trouble coordinating movements. Specific symptoms include: - Difficulty walking - Muscle weakness - Speech problems - Involuntary eye movements - Scoliosis (curving of the spine to one side) - Heart palpitations, from the heart disease which can happen along with Friedreich ataxia People with Friedreich ataxia usually need a wheelchair 15 to 20 years after symptoms first appear. In severe cases, people become incapacitated. There is no cure. You can treat symptoms with medicines, braces, surgery, and physical therapy. NIH: National Institute of Neurological Disorders and Stroke
US source; availability in Australia may differ.
Source: MedlinePlus Health Topics (medlineplus.gov), public domain (U.S. National Library of Medicine). Read the full source.
Sources and dates
- ClinicalTrials.gov – trial records, statuses and site lists
- MedlinePlus – the About text above, reproduced exactly
- Orphanet / Orphadata – prevalence, age of onset, inheritance, genes and alternative names, used under CC BY 4.0
- ClinicalTrials.gov processing date: 1 September 2026.
- This page last checked by Voxsanity: 11 October 2026.
Voxsanity reformats data from public registries into this layout. It does not edit, interpret or add to what the registry published.
Not medical advice.
Individual trial records are refreshed on a rolling basis rather than all at once, so a record may be up to several weeks old. Each trial page and trial card shows the date its own record was last synced. Where a record has lagged, its status, sites and enrolment can differ from the current registry state in either direction, so check the registry link on the trial page before acting on them.
Orphanet citation
Orphadata Science: Free access data from Orphanet. © INSERM 1999. Available on https://www.orphadata.com. Used under CC BY 4.0. Source: Orphanet / Orphadata (orphadata.com). Accessed 20 September 2026.
Friedreich Ataxia is one of the rare diseases tracked on the Voxsanity rare disease hub, where you can compare it with every other rare condition we follow and filter trials by country.
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