Phase 2 Sickle Cell Disease Trial, Completed NCT00004412 Sponsor: Susan P. Perrine Condition: Sickle Cell Disease
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Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial looked at a treatment called Arginine Butyrate (given through a drip into a vein) compared with standard local wound dressings, for people with leg or skin ulcers. A total of 23 participants started the first phase of the trial — 11 in the standard dressing group and 12 in the Arginine Butyrate group. The trial then had a crossover phase, where some participants from the standard dressing group could switch to the Arginine Butyrate treatment. The main thing the trial was measuring was whether an ulcer shrank by at least 25% of its original size, which was counted as "healed" for the purposes of this study. The reported data shows that, for the primary measure (ulcer shrinking by at least 25%), 24% of ulcers in the standard local care dressing group met this threshold, compared with 78% in the Arginine Butyrate group. For the secondary measure — the percentage of ulcers that closed completely within three months — the reported figures were 8% in the standard dressing group and 31% in the Arginine Butyrate group. These are the numbers as submitted to the registry; no further breakdown by individual patient characteristics was reported in the data provided. These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 2 Sickle Cell Disease Trial, Completed

NCT00004412
Completed Phase 2

voxsanity.com.au · Eligibility summary from public government registries · 18 August 2026 · not medical advice

Who may and may not be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who may be able to join

  • You have been diagnosed with a significant sickle cell condition, including Hemoglobin SS, Hemoglobin S-beta thalassemia, or a related hemoglobin variant
  • You are between 16 and 60 years old
  • You have one or more ulcers on your lower leg or ankle that have not healed for at least 6 months
  • Your liver is functioning normally, with liver enzyme levels at or below 250 IU
  • Your kidneys are functioning normally, with creatinine levels at or below 1.2 mg/mL (for adults) or 0.9 mg/mL (for teenagers)
  • If you have a skin infection (cellulitis) or other infection around the ulcer, you must have received antibiotic treatment for it before joining the trial

Who may not be able to join

Each point below is a reason the trial team may not be able to accept someone. It is not a list of requirements to meet.

  • You are pregnant
  • You are able to have children but are not using effective birth control
  • You have liver problems or abnormal liver enzyme levels above 250 IU
  • You have kidney problems or creatinine levels above 1.2 mg/mL (adults) or 0.9 mg/mL (teenagers)
  • You are currently receiving regular blood transfusions as an ongoing treatment
  • You have had or are currently receiving chemotherapy for cancer
  • You are currently taking a type of medication called butyrate derivatives (confirm with trial site)
  • You are currently taking steroid medications (corticosteroids)
  • You have seizures that are not well controlled by treatment
  • You have another condition that may weaken your immune system

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 17 August 2026

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Trial details

Status
Completed
Phase
Phase 2
Sponsor
Susan P. Perrine
Registry
ClinicalTrials.gov
Start date
1 September 1997
Est. completion
1 December 2002

Where this trial was run

🇺🇸 United States

These are the locations recorded on the registry, and they are a historical record: this trial is not enrolling, so they are not places you can join it.

Primary endpoints

Healing Defined as a Decrease in Ulcer Area by at Least 25% of the Initial Area

Other options

Expanded access pathways

This trial is not enrolling. Other access pathways exist in general: in Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients. Whether it applies to any treatment studied here is a question for your doctor — nothing on this page says it does.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 17 August 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov