Phase 2 Huntington's Disease Trial, Terminated NCT04617860 Sponsor: Wave Life Sciences USA, Inc. Condition: Huntington's Disease
Back to Huntingtons Disease

Trial results

AI generated results summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

According to the results reported on ClinicalTrials.gov, this trial tested a drug called WVE-120102 in 36 people across three starting dose groups — 8 people began on 4 mg, 10 on 8 mg, and 18 on 16 mg. During the trial, many participants had their doses increased over time, with some eventually receiving 32 mg. The trial was measuring safety and tolerability — in other words, it was tracking what kinds of unwanted health events occurred while people were taking the drug and at what doses. Notably, none of the 36 participants completed the trial; all either withdrew or did not finish for other reasons. The reported data shows that across all dose groups, a number of participants experienced what are called "treatment-emergent adverse events" (TEAEs) — these are unwanted health events that occurred during the treatment period. In the 4 mg group, 7 out of 8 participants had at least one such event; in the 8 mg group, 14 participants; in the 16 mg group, 34 participants; and in the 32 mg group, 17 participants. The reported data also shows that more severe events were recorded at higher doses — no participants in the 4 mg or 8 mg groups had a severe event, while 2 in the 16 mg group and 5 in the 32 mg group did. Serious adverse events (a specific medical category for events requiring significant attention) were reported in 0, 1, 5, and 3 participants across the four dose groups respectively. A total of 4 participants withdrew from the trial due to these events (0, 1, 3, and 0 across the dose groups). These are the results as reported to ClinicalTrials.gov. They are not medical advice — always discuss what they mean for you with your doctor.

These are the results as reported to ClinicalTrials.gov, not medical advice. Verify independently with the trial site and discuss what they mean for you with your doctor.

Phase 2 Huntington's Disease Trial, Terminated

NCT04617860
Terminated Phase 2 🇦🇺 Australian site

Who may be able to join

AI generated eligibility summary. Written by an AI model from the official source data and checked on a sample basis. It can contain mistakes, so confirm anything important against the original source. How we use AI

Who might be able to join this trial:

  • You previously completed the earlier phase of this study (called WVE-HDSNP2-001) using the drug WVE-120102.

Who may not be able to join:

  • You have taken another experimental drug (other than WVE-120102) in the past year, or within a certain period based on how long that drug stays in your body — whichever is longer.
  • You are unable to have a brain MRI scan, even with the help of sedation (medication to help you relax or sleep during the scan).
  • You have a significant health condition other than Huntington's disease that the study doctor believes would make it unsafe or difficult for you to complete the study.

Important: Always verify eligibility with the trial site directly before applying.

Based on publicly available eligibility criteria from ClinicalTrials.gov. Verify directly with the trial site before acting. This is not medical advice.

This is a simplified plain English summary of the eligibility criteria. Full criteria are set by the trial investigators and may include additional requirements not shown here. Never self-exclude from a trial based on this summary. Contact the trial site directly to confirm your eligibility.
Last synced 28 July 2026
Phase 2: approximately ~30% of drugs entering this phase reach regulatory approval, based on published industry-wide historical data. This is not specific to this trial.
Phase success rates shown are historical industry-wide averages based on published data. They are not a prediction for this specific trial or your individual situation.

Contact this trial

Principal Investigator: Medical Director, MD, WAVE Life Sciences

Australian sites

Westmead Hospital, Sydney, New South Wales
Royal Brisbane & Women's Hospital, Herston, Queensland
Royal Melbourne Hospital, Carlton, Victoria
Monash Health, Clayton, Victoria
Alfred Health, Melbourne, Victoria
Calvary Health Care Bethlehem, Parkdale, Victoria
North Metropolitan Health Service, Perth, Western Australia

Contact details sourced from ClinicalTrials.gov. Verify directly with the trial site before attending.

GP referral letter

Print a one-page summary to share with your doctor.

Trial details

Status
Terminated
Phase
Phase 2
Sponsor
Wave Life Sciences USA, Inc.
Registry
ClinicalTrials.gov
Start date
24 September 2019
Est. completion
29 April 2021

Where this trial is recruiting

🇦🇺 Australia 🇨🇦 Canada 🇩🇰 Denmark 🇫🇷 France 🇩🇪 Germany 🇵🇱 Poland 🇬🇧 United Kingdom

7 site(s) in Australia. Confirm current status and contact details directly with the trial site.

Primary endpoints

Safety: Number of Patients With Treatment-emergent Adverse Events (TEAEs); Safety: Number of Patients With a Severe TEAE; Safety: Number of Patients With Serious TEAEs; Safety and Tolerability: Number of Patients Who Withdraw Due to TEAEs

Can't join this trial?

Expanded access pathways

If this trial is not available to you, other access pathways may exist. In Australia, the TGA Special Access Scheme allows access to unapproved therapeutic goods for individual patients.

TGA Special Access Scheme information

Find other recruiting trials on ClinicalTrials.gov

Data last synced from ClinicalTrials.gov: 28 July 2026. Trial status can change. Always verify current status directly with the trial site before making any decision.

Trial recruitment status can change without notice between our nightly data updates. Always contact the trial site directly to confirm current recruitment status before making any decisions or travel arrangements.

View original record on ClinicalTrials.gov